Abstract
Background
Allogeneic stem cell transplant is the only curative treatment for Wiskott-Aldrich syndrome.
Case characteristics
18-months-old boy with no sibling, cord blood or matched unrelated donor transplant options.
Outcome
Doing well 7 years after haploidentical stem cell transplantation using unmanipulated bone marrow as the stem cell source.
Message
Father as a haplo-identical donor is a feasible option.
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References
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John, M.J., Philip, C.C., Mathew, A. et al. Un-manipulated haploidentical transplant in Wiskott-Aldrich syndrome. Indian Pediatr 54, 327–328 (2017). https://doi.org/10.1007/s13312-017-1097-z
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DOI: https://doi.org/10.1007/s13312-017-1097-z